Set to enter larger trial across 5 countries, it works by permanently turning off gene that causes high bad cholesterol ...

Typically, the goal of ALS treatments is to slow the disease or halt progression. But new data from the antisense oligonucleotide (ASO) jacifusen for FUS-ALS show that two patients went beyond the ...

Some patients with a rare form of ALS benefited from an experimental therapy, with biomarker evidence of reduced injury to neurons and even limited functional recovery.

An experimental antibiotic zosurabalpin to fight deadly superbug has entered the final human trials. This development could ...

SB 535 formally paves the way for health care clinics to become 'experimental treatment centers' that can provide drugs still ...

An experimental painkiller could be the key to solving the opioid epidemic - The drug could offer powerful pain relief ...

An experimental drug known as ulefnersen has shown remarkable efficacy in treating a rare, aggressive form of ALS ...

When Columbia neurologist and scientist Neil Shneider speaks to his ALS patients who volunteer for experimental therapies, he ...

Right to Try laws are being adopted and expanded throughout the country. In one state, they’ll allow healthy people to access ...

An experimental drug developed at Duke University School of Medicine could offer powerful pain relief without the dangerous ...

A medical revolution quietly unfolds on Hainan, allowing patients to access cutting-edge therapies before they hit the market ...

From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing. Whether it's investigating the financials of Elon Musk's pro-Trump PAC or ...