News

The city of Rockford dedicated a memorial plaque to one of their own, who died in November to a form of muscular dystrophy.
The FDA’s shift on Elevidys sends a message: boldness, scientific rigor and urgency are essential in confronting rare ...
Insmed’s (INSM) treatment of Duchenne muscular dystrophy, the single-stranded, non-replicating, recombinant adeno-associated virus serotype 9 ...
Echocardiography may be at the vanguard for early and rapid detection of heart issues indicative of Duchenne muscular ...
The first few months of 2025 brought hope to the rare disease community. Food and Drug Administration leadership promised ...
Keros Therapeutics, Inc. ('Keros”) (Nasdaq: KROS), a clinical-stage biopharmaceutical company focused on developing and ...
This weekend, the Rockford community will come together once again for the 27th Annual Mitchell's Run Thru Rockford (MRTR), a USATF-certified 5K run/walk and Kids K benefiting Parent Project Muscular ...
Avidity Biosciences surges 36% on reports that Novartis may eye a deal, with talks said to be early and interest from other suitors possible.
The event is named after Mitchell Peterson, who had Duchenne muscular dystrophy.
After deaths and FDA setbacks, Sarepta abandoned LGMD gene therapy, leaving families desperate and patients without ...
US FDA grants orphan drug designation to Keros Therapeutics’ KER-065 to treat Duchenne muscular dystrophy: Lexington, Massachusetts Friday, August 22, 2025, 15:00 Hrs [IST] Kero ...