It's been nearly two years since Elevidys, a gene therapy for Duchenne MD developed by Sarepta Therapeutics, was approved by ...

RNS60 was well tolerated when inhaled twice daily at home as part of an expanded access program (EAP) for people with ...

Assessing multiple sclerosis disease activity using the MSDA blood biomarker test can help guide decisions about care, per a study.

Comprehensive Analysis of the Global Clinical Trials IndustryThe global clinical trials sector is experiencing a significant ...

Data from the BroADen Phase 1b atopic dermatitis (AD) patient trial expected to be reported in 4Q25Completed SAD/MAD dosing in KT-621 Phase 1 ...

Cholesterol is a type of fat found in your blood and is essential for the body to function properly, but having high ...

Unsupervised use of psilocybin has risen dramatically among youth and adults 30 and older, along with a corresponding rise in ...

Supporters will unite on May 5 to mark World Pulmonary Hypertension Day, with a focus this year on early diagnosis.

Seattle Children’s created a clinical effectiveness program under its center of quality to look up all medical literature available for tough questions. The program includes millions of pieces of ...

Rituximab, a lower-cost treatment, may be as effective at managing RRMS as the approved therapy Ocrevus, a new study from ...

Testing SMA patient DNA with advanced methods like HapSMA can reveal genetic changes that affect how severe the disease is, ...

Matter of Time,” a documentary featuring legendary rocker Eddie Vedder premiering this fall at the Tribeca Film Festival, is ...