Certain proteins implicated in immune response and the body's process to stop bleeding may be biomarkers of BMD progression, ...

The first few months of 2025 brought hope to the rare disease community. Food and Drug Administration leadership promised ...

Insmed’s (INSM) treatment of Duchenne muscular dystrophy, the single-stranded, non-replicating, recombinant adeno-associated virus serotype 9 ...

The agency said it had become aware of more reports of serious adverse events, leading center director Vinay Prasad to ...

This September, the Muscular Dystrophy Association (MDA) is launching its milestone #MDAstrong campaign during a historic moment for the organization: its 75th anniversary. The campaign reframes what ...

The event is named after Mitchell Peterson, who had Duchenne muscular dystrophy.

On the flip side, this has also led to many great movies becoming sadly forgotten, washed out of popular memory by the ...

The city of Rockford dedicated a memorial plaque to one of their own, who died in November to a form of muscular dystrophy.

CureDuchenne, a global nonprofit based in Newport Beach that is dedicated to funding and finding a cure for Duchenne muscular ...

Sarcomatrix Therapeutics, a biopharmaceutical company developing small‑molecule treatments for Duchenne muscular dystrophy (DMD), today announced it has received a $300,000 investment from Nevada’s ...