The report also provides a detailed analysis of the current Niemann-Pick disease type C marketed drugs and late-stage pipeline drugs. BROOKLYN, BROOKLYN, UNITED STATES, June 25, 2025 /EINPresswire.com ...

US biotech BioMarin Pharmaceutical (Nasdaq: BMRN) has presented new five-year data from its pivotal Phase III trial of ...

A recent study led by the Indian Council of Medical Research (ICMR) has found that a low dose of emicizumab could be as ...

In Hooghly district, haemophilia injections have not been available at either Chinsurah Imambara Hospital or Arambagh Medical ...

Many with hemophilia endure infantilizing by caregivers, most of it unintentional. Columnist Alliah Czarielle describes how to avoid this.

Elton John and Jeanine White, the mother of Ryan White, urge Congress not to cut funding for lifesaving HIV and AIDS programs ...

Directly switching from Hemlibra to Mim8 was well tolerated in people with hemophilia A, with or without inhibitors, a study ...

Sangamo Therapeutics’ investigational gene therapy appears to improve kidney function at 52 weeks for patients with a rare genetic disorder.  | Sangamo Therapeutics’ investigational gene therapy ...

Strong efficacy and cardiovascular benefits should allow Novo to continue growing sales of GLP-1 therapies in diabetes. While Novo lost share to Eli Lilly's once-weekly Trulicity, Ozempic and Rybelsus ...

Columnist G Shellye Horowitz struggles to find care for her gastrointestinal issues due to the shortage of medical providers ...

Medical gaslighting is far too common, columnist Jennifer Lynne says. We all deserve to have our symptoms taken seriously.

Sanofi’s SNY stock has been trading below its 200-day and 50-day moving averages since early June. On June 23, the stock’s ...